Human pluripotent stem cell (hPSC)-derived models for autism spectrum disorder drug discovery DOI
Lingdi Nie, Courtney Irwin,

Sarah Geahchan

и другие.

Expert Opinion on Drug Discovery, Год журнала: 2024, Номер unknown, С. 1 - 19

Опубликована: Дек. 24, 2024

Autism spectrum disorder (ASD) is a prevalent and complex neurodevelopmental (NDD) with genetic environmental origins. Currently, there are no effective pharmacological treatments targeting core ASD features. This leads to unmet medical needs of individuals requires relevant human disease models recapitulating clinical heterogeneity better understand underlying mechanisms identify potential therapies. Recent advancements in stem cell technology have enabled the generation pluripotent (hPSC)-derived two-dimensional (2D) three-dimensional (3D) neural models, which serve as powerful tools for modeling drug discovery.

Язык: Английский

Assembloid models of cell-cell interaction to study tissue and disease biology DOI
Massimo M. Onesto, Ji‐il Kim, Sergiu P. Paşca

и другие.

Cell stem cell, Год журнала: 2024, Номер 31(11), С. 1563 - 1573

Опубликована: Окт. 24, 2024

Язык: Английский

Процитировано

13

Modelling human brain development and disease with organoids DOI
Marcella Birtele, Madeline A. Lancaster, Giorgia Quadrato

и другие.

Nature Reviews Molecular Cell Biology, Год журнала: 2024, Номер unknown

Опубликована: Дек. 12, 2024

Язык: Английский

Процитировано

11

Organoid intelligence for developmental neurotoxicity testing DOI Creative Commons

Dowlette-Mary Alam El Din,

Jeongwon Shin,

Alexandra Lysinger

и другие.

Frontiers in Cellular Neuroscience, Год журнала: 2024, Номер 18

Опубликована: Окт. 8, 2024

The increasing prevalence of neurodevelopmental disorders has highlighted the need for improved testing methods to determine developmental neurotoxicity (DNT) hazard thousands chemicals. This paper proposes integration organoid intelligence (OI); leveraging brain organoids study neuroplasticity in vitro, into DNT paradigm. OI brings a new approach measure impacts xenobiotics on plasticity mechanisms – critical biological process that is not adequately covered current vitro assays. Finally, artificial (AI) techniques will further facilitate analysis complex data these mechanisms.

Язык: Английский

Процитировано

4

Assessing the Utility of Organoid Intelligence: Scientific and Ethical Perspectives DOI Creative Commons
Michael W. Nestor, Richard L. Wilson

Organoids, Год журнала: 2025, Номер 4(2), С. 9 - 9

Опубликована: Май 1, 2025

The development of brain organoids from human-induced pluripotent stem cells (iPSCs) has expanded research into neurodevelopment, disease modeling, and drug testing. More recently, the concept organoid intelligence (OI) emerged, proposing that these constructs could evolve to support learning, memory, or even sentience. While this perspective driven enthusiasm in field suggested new applications fields such as neuromorphic computing, it also introduces significant scientific conceptual concerns. Current lack anatomical complexity, network organization, sensorimotor integration necessary for Despite this, claims surrounding OI often rely on oversimplified interpretations neural activity, fueled by neurorealist reification biases misattribute neurophysiological properties biologically limited systems. Beyond limitations, framing risks imposing ethical regulatory challenges based speculative concerns rather than empirical evidence. assumption might possess sentience, develop over time, lead unnecessary restrictions legitimate while misrepresenting their actual capabilities. Additionally, comparing biological systems silicon-based computing overlooks fundamental differences scalability, efficiency, predictability, raising questions about whether can meaningfully contribute computational advancements. must recognize limitations models prematurely defining a distinct domain. A more cautious, evidence-driven approach is ensure remain valuable tools neuroscience without overstating potential. To maintain credibility public trust, essential separate narratives grounded research, thus allowing continued progress studies reinforcing misconceptions

Язык: Английский

Процитировано

0

Protocol for generating human assembloids to investigate thalamocortical and corticothalamic synaptic transmission and plasticity DOI Creative Commons

Anjana Nityanandam,

Mary H. Patton,

Ildar T. Bayazitov

и другие.

STAR Protocols, Год журнала: 2025, Номер 6(1), С. 103630 - 103630

Опубликована: Фев. 7, 2025

Язык: Английский

Процитировано

0

Modeling forebrain regional development and connectivity by human brain organoids DOI

Mu Seog Choe,

Cynthia Lo,

In‐Hyun Park

и другие.

Current Opinion in Genetics & Development, Год журнала: 2025, Номер 91, С. 102324 - 102324

Опубликована: Фев. 20, 2025

Язык: Английский

Процитировано

0

Role of Post-Transcriptional Regulation in Learning and Memory in Mammals DOI Open Access
Carlo Maria Di Liegro, Gabriella Schiera,

Giuseppe Schirò

и другие.

Genes, Год журнала: 2024, Номер 15(3), С. 337 - 337

Опубликована: Март 5, 2024

After many decades, during which most molecular studies on the regulation of gene expression focused transcriptional events, it was realized that post-transcriptional control equally important in order to determine where and when specific proteins were be synthesized. Translational is importance brain, all steps mRNA maturation, transport different regions cells actual expression, response signals, constitute basis for neuronal plasticity and, as a consequence, structural stabilization/modification synapses; notably, these latter events are fundamental highest brain functions, such learning memory, characterized by long-term potentiation (LTP) synapses. Here, we will discuss bases considering both role RNA-binding (RBPs) effects non-coding RNAs involved controlling splicing, editing, stability translation mRNAs. Importantly, has also been found dysregulation metabolism/localization pathological conditions, arising either development or adult nervous system.

Язык: Английский

Процитировано

2

Human pluripotent stem cell (hPSC)-derived models for autism spectrum disorder drug discovery DOI
Lingdi Nie, Courtney Irwin,

Sarah Geahchan

и другие.

Expert Opinion on Drug Discovery, Год журнала: 2024, Номер unknown, С. 1 - 19

Опубликована: Дек. 24, 2024

Autism spectrum disorder (ASD) is a prevalent and complex neurodevelopmental (NDD) with genetic environmental origins. Currently, there are no effective pharmacological treatments targeting core ASD features. This leads to unmet medical needs of individuals requires relevant human disease models recapitulating clinical heterogeneity better understand underlying mechanisms identify potential therapies. Recent advancements in stem cell technology have enabled the generation pluripotent (hPSC)-derived two-dimensional (2D) three-dimensional (3D) neural models, which serve as powerful tools for modeling drug discovery.

Язык: Английский

Процитировано

0