Exo-Linker: Positional Reconfiguration Driving Significant Advances in ADC Stability and Efficacy DOI Open Access

Tomohiro Watanabe,

Tomohiro Fujii,

Yutaka Matsuda

и другие.

ADC Review / Journal of Antibody-drug Conjugates, Год журнала: 2024, Номер unknown

Опубликована: Дек. 30, 2024

Antibody-drug conjugates (ADCs) have transformed targeted cancer therapy by combining the specificity of monoclonal antibodies with cytotoxic potency small-molecule drugs. However, payload instability, hydrophobicity, and premature cleavage limit their efficacy safety. This study presents Exo-Linker technology as a novel solution to these issues. By repositioning cleavable peptide linkers like Glu-Val-Cit Glu-Glu-Val-Cit at exo-position p-aminobenzyl carbamate moiety, Exo-Linkers improve stability, hydrophilicity, resistance enzymatic degradation. Key findings highlight superior pharmacokinetics, tumor-suppressive efficacy, stability ADCs in preclinical models, significantly outperforming traditional Val-Cit-based linkers. Integration second-generation AJICAP platform broadens therapeutic windows, ensures precise drug-to-antibody ratio control, minimizes aggregation. establish new standard for ADC development, overcoming critical limitations while enabling safer more effective treatments. innovative approach redefines landscape, enhances patient outcomes, scope applications.

Язык: Английский

Understanding the Toxicity Profile of Approved ADCs DOI Creative Commons
P Martínez,

Alfonso López de Sá,

Cristina Díaz‐Tejeiro

и другие.

Pharmaceutics, Год журнала: 2025, Номер 17(2), С. 258 - 258

Опубликована: Фев. 14, 2025

Background: Antibody-drug conjugates (ADCs) represent a novel therapeutic class that combines an antibody against tumor-associated antigen (TAA), payload, and linker binds these two components. Serious adverse events (SAEs), particularly those of grade 3 (G3) or higher, frequently contribute to the abandonment ADCs during clinical development. Methods: In this study, we analyzed toxicity profiles all approved ADCs, aiming uncover correlations between their safety specific characteristics Results: our analysis, dose reductions, delays, treatment discontinuations, ≥G3 toxicities were not significantly different across payload types. Similarly, no association was found mechanism action toxicities, including anemia, neutropenia, febrile thrombocytopenia, diarrhea. By exploring observed by organ, identified most related action, like diarrhea in 10% patients treated with sacituzumab govitecan (the SN-38 is active metabolite irinotecan), very few presence TAA normal tissue (presence Nectin-4 skin rash 14% enfortumab vedotin). line this, major differences studies levels (trastuzumab deruxtecan Destiny Breast Studies HER2 expression levels). Conclusions: Our analysis reveals ADC are driven payload's effects on non-transformed tissues; however, detailed each component should be taken into consideration.

Язык: Английский

Процитировано

1

Antibody-drug conjugates in breast cancer treatment: resistance mechanisms and the role of therapeutic sequencing DOI Open Access
Éric Larose,

Xinying Hua,

Silin Yu

и другие.

Cancer Drug Resistance, Год журнала: 2025, Номер unknown

Опубликована: Март 6, 2025

Antibody-drug conjugates (ADCs) are a transformative approach in breast cancer therapy, offering targeted treatment with reduced toxicity by selectively delivering cytotoxic agents to cells. While ADCs like trastuzumab emtansine (T-DM1), deruxtecan (T-DXd), and sacituzumab govitecan have shown significant efficacy, resistance mechanisms such as antigen loss, impaired internalization, efflux of payloads challenge their effectiveness. This review discusses these explores advanced strategies overcome them, including innovations linker chemistry, multi-antigen targeting, biomarker-driven personalization. Additionally, therapeutic sequencing - determining the optimal order other treatments chemotherapy, endocrine immunotherapy is examined crucial maximize ADC efficacy manage resistance. Evidence-based strategies, particularly for human epidermal growth factor receptor 2 (HER2)-positive triple-negative (TNBC), supported clinical trials demonstrating benefits both early-stage metastatic settings. The potential combination therapies, immune checkpoint inhibitors (ICIs), further highlights evolving landscape treatment. As technology advances, personalized approaches integrating biomarkers optimized protocols offer promising avenues enhance outcomes combat cancer.

Язык: Английский

Процитировано

0

Structural Insights into Lipoate Ligase A-Mediated Antibody Modifications DOI
Kazutoshi Takahashi, Shunsuke Yamazaki, Yutaka Matsuda

и другие.

Biochemistry, Год журнала: 2025, Номер unknown

Опубликована: Март 20, 2025

Enzyme-mediated site-specific protein modification is gaining attention in biopharmaceuticals due to its high specificity and mild conditions. Lipoic acid ligase A (LplA) has been widely studied for conjugating short-chain fatty acids lysine residues, traditionally using LAP tags. Recent advances have enabled tag-free LplA modifications, expanding applications antibody-drug conjugates (ADCs) beyond. This study investigates the selective of Lys188 trastuzumab by LplA. Spatial analysis molecular modeling suggest that D151 H189 facilitate nucleophilic attack stabilize intermediates via electrostatic π-cation interactions. These insights enhance our understanding enzyme-driven site selectivity, guiding rational design antibody modifications. The findings support broader ADC production, diagnostics, next-generation biopharmaceuticals, emphasizing role local amino environments enzymatic

Язык: Английский

Процитировано

0

Current advances in separation chemistry for antibody purification and analysis DOI Open Access

Suprit Deol,

Yutaka Matsuda, Yuki Hiruta

и другие.

Analytical Sciences, Год журнала: 2025, Номер unknown

Опубликована: Март 24, 2025

Язык: Английский

Процитировано

0

Exo-Cleavable Linkers: Enhancing Stability and Therapeutic Efficacy in Antibody-Drug Conjugates DOI Creative Commons

Tomohiro Watanabe,

Tomohiro Fujii,

Yutaka Matsuda

и другие.

Journal of Synthetic Organic Chemistry Japan, Год журнала: 2024, Номер 82(11), С. 1117 - 1124

Опубликована: Ноя. 1, 2024

Customized drug delivery systems are essential for precision medicine, with antibody-drug conjugates (ADCs) representing a pivotal approach that integrates cytotoxic payloads monoclonal antibodies (mAbs) through sophisticated chemical linkers. However, optimizing ADC stability while achieving controlled payload release remains challenging. The FDA-approved valine-citrulline (Val-Cit) linker commonly used in ADCs, suffers from issues such as hydrophobicity-induced aggregation, limited drug-antibody ratio (DAR), and premature release.

Язык: Английский

Процитировано

2

Safety Concerns in Neurological Clinical Trials: A Challenge That the FDA Must Resolve DOI Creative Commons
Sarfaraz K. Niazi

Biomedicines, Год журнала: 2024, Номер 12(12), С. 2918 - 2918

Опубликована: Дек. 22, 2024

Background: Monoclonal antibodies approved by the FDA, lecanemab, donanemab, and aducanumab, are failing to meet expected efficacy treat early Alzheimer’s disease, aducanumab has been recalled. Methods: Recently, it was reported that clinical trials of these may have violated patient’s rights subjected them high, likely lethal risk. The challenge with developing neurological disorders is their poor blood–brain barrier (BBB) penetration if antibody must enter brain, resulting in almost negligible brain bioavailability, requiring high dosing can be toxic. Results: drugs should also reviewed, considering placebo effects, since all shown severe side effects not prevented responses. In this critical urgent advice I am suggesting a guideline amendment proof sufficient bioavailability at site action, where known. Conclusions: For cross barrier, there proven options such as conjugating transferrin protein, making its absence more questionable.

Язык: Английский

Процитировано

2

Antibody Modification via Lipoic Acid Ligase A‐Mediated Site‐Specific Labeling DOI
Shunsuke Yamazaki, Yutaka Matsuda

Chemistry & Biodiversity, Год журнала: 2024, Номер unknown

Опубликована: Окт. 22, 2024

Abstract Enzymatic modification, particularly utilizing lipoic acid ligase (LplA), has emerged as a transformative approach in biopharmaceuticals, enabling precise and site‐specific protein modifications. This review delves into the innovative applications of LplA antibody modifications, including creation antibody‐drug conjugates (ADCs) advancement tag‐free conjugation techniques. LplA's ability to facilitate incorporation bioorthogonal groups its adaptability various substrates underscores versatility. Key developments include successful generation dual‐labeled antibodies application modifying fragments. Additionally, explores potential for enhance therapeutic efficacy ADCs through improved drug‐to‐antibody ratios payload attachment. The implications these advancements are significant, suggesting that LplA‐mediated modifications could lead more effective targeted antibody‐based therapies. aims provide comprehensive overview role expanding possibilities enzymatic conjugation, setting stage future research clinical applications.

Язык: Английский

Процитировано

1

Immunoconjugates as an Efficient Platform for Drug Delivery: A Resurgence of Natural Products in Targeted Antitumor Therapy DOI Creative Commons
Rositsa Mihaylova, Denitsa Momekova,

Viktoria Elincheva

и другие.

Pharmaceuticals, Год журнала: 2024, Номер 17(12), С. 1701 - 1701

Опубликована: Дек. 17, 2024

The present review provides a detailed and comprehensive discussion on antibody–drug conjugates (ADCs) as an evolving new modality in the current therapeutic landscape of malignant diseases. principle concepts targeted delivery highly toxic agents forsaken stand-alone drugs are examined detail, along with biochemical technological tools for their successful implementation. An extensive analysis ADCs’ major components is conducted parallel function impact stability, efficacy, safety, resistance profiles immunoconjugates. scope article covers classes currently validated natural compounds used payloads, emphasis structural mechanistic features, origin, distribution. Future perspectives design thoroughly explored, addressing inherent or emerging challenges limitations. survey also overview molecular rationale active tumor targeting ADC-based platforms, exploring cellular biology clinical relevance markers “homing” mechanism both hematological solid malignancies.

Язык: Английский

Процитировано

0

Exo-Linker: Positional Reconfiguration Driving Significant Advances in ADC Stability and Efficacy DOI Open Access

Tomohiro Watanabe,

Tomohiro Fujii,

Yutaka Matsuda

и другие.

ADC Review / Journal of Antibody-drug Conjugates, Год журнала: 2024, Номер unknown

Опубликована: Дек. 30, 2024

Antibody-drug conjugates (ADCs) have transformed targeted cancer therapy by combining the specificity of monoclonal antibodies with cytotoxic potency small-molecule drugs. However, payload instability, hydrophobicity, and premature cleavage limit their efficacy safety. This study presents Exo-Linker technology as a novel solution to these issues. By repositioning cleavable peptide linkers like Glu-Val-Cit Glu-Glu-Val-Cit at exo-position p-aminobenzyl carbamate moiety, Exo-Linkers improve stability, hydrophilicity, resistance enzymatic degradation. Key findings highlight superior pharmacokinetics, tumor-suppressive efficacy, stability ADCs in preclinical models, significantly outperforming traditional Val-Cit-based linkers. Integration second-generation AJICAP platform broadens therapeutic windows, ensures precise drug-to-antibody ratio control, minimizes aggregation. establish new standard for ADC development, overcoming critical limitations while enabling safer more effective treatments. innovative approach redefines landscape, enhances patient outcomes, scope applications.

Язык: Английский

Процитировано

0