Innovative Drug Discovery: Targeting Cancer, Neurological Disorders, and Obesity DOI Creative Commons
Robert B. Kargbo

ACS Medicinal Chemistry Letters, Год журнала: 2024, Номер 15(9), С. 1440 - 1442

Опубликована: Авг. 21, 2024

The landscape of therapeutic innovation is rapidly evolving, with significant advances in cancer treatment, obesity management, and the modulation protein interactions neurodegenerative disorders. This Patent Highlight explores scientific breakthroughs described four recent patents covering novel compounds, advanced methods for identifying E3 ligase substrates, developing new strategies combating its related metabolic These innovations, focusing on specific molecular targets pathways, promise more effective personalized treatment options, addressing unmet needs oncology, neurology, health.

Язык: Английский

Deleterious coding variation associated with autism is consistent across populations, as exemplified by admixed Latin American populations DOI Creative Commons

Marina Natividad Avila,

Seulgi Jung, F. Kyle Satterstrom

и другие.

medRxiv (Cold Spring Harbor Laboratory), Год журнала: 2025, Номер unknown

Опубликована: Янв. 6, 2025

The past decade has seen remarkable progress in identifying genes that, when impacted by deleterious coding variation, confer high risk for autism spectrum disorder (ASD), intellectual disability, and other developmental disorders. However, most underlying gene discovery efforts have focused on individuals of European ancestry, limiting insights into genetic risks across diverse populations. To help address this, the Genomics Autism Latin American Ancestries Consortium (GALA) was formed, presenting here largest sequencing study ASD (n>15,000). We identified 35 genome-wide significant (FDR < 0.05) genes, with substantial overlap findings from cohorts, highly constrained showing consistent signal results provide support emerging (e.g., MARK2 , YWHAG PACS1 RERE, SPEN, GSE1, GLS, TNPO3, ANKRD17 ) established utility testing approaches variants populations, while also demonstrating ongoing need more inclusive research testing. conclude that biology is universal not to any detectable degree ancestry. Branko Aleksic, Mykyta Artomov, Mafalda Barbosa, Elisa Benetti, Catalina Betancur, Monica Biscaldi-Schafer, Anders D. Børglum, Harrison Brand, Alfredo Brusco, Joseph Buxbaum, Gabriele Campos, Simona Cardaropoli, Diana Carli, Angel Carracedo, Marcus C. Y. Chan, Andreas G. Chiocchetti, Brian H. Chung, Brett Collins, Ryan L. Edwin Cook, Hilary Coon, Claudia I. S. Costa, Michael Cuccaro, David J. Cutler, Mark Daly, Silvia De Rubeis, Bernie Devlin, N. Doan, Enrico Domenici, Shan Dong, Chiara Fallerini, Magdalena Fernandez, Montserrat Fernández-Prieto, Giovanni Battista Ferrero, Eugenio Ferro, Jennifer Foss Feig, Christine M. Freitag, Jack Fu, Liliana Galeano, Jay Gargus, Sherif Gerges, Giorgio, Ana Cristina Girardi, Stephen Guter, Emily Hansen-Kiss, Erina Hara, Danielle Halpern, Gail E. Herman, Luis Hernandez, Irva Hertz-Picciotto, Hougaard, Christina Hultman, Suma Jacob, Miia Kaartinen, Lambertus Klei, Alexander Kolevzon, Itaru Kushima, Maria Lattig, So Lun Lee, Terho Lehtimäki, Lindsay Liang, Carla Lintas, Alicia Ljungdahl, Andrea del Pilar Lopez, Caterina Lo Rizzo, Yunin Ludena, Patricia Maciel, Behrang Mahjani, Nell Maltman, Marianna Manara, Dara Manoach, Dalia Marquez, Gal Meiri, Idan Menashe, Judith Miller, Nancy Minshew, Matthew Mosconi, Marina Natividad Avila, Rachel Nguyen, Norio Ozaki, Aarno Palotie, Mara Parellada, Rita Passos-Bueno, Lisa Pavinato, Katherine P. Peña, Minshi Peng, Margaret Pericak-Vance, Antonio Persico, Isaac Pessah, Thariana Pichardo, Kaija Puura, Abraham Reichenberg, Alessandra Renieri, Kathryn Roeder, Catherine Sancimino, Stephan Sanders, Sven Sandin, F. Kyle Satterstrom, W. Scherer, Sabine Schlitt, Rebecca Schmidt, Lauren Schmitt, Katja Schneider-Momm, Paige Siper, Laura Sloofman, Moyra Smith, Renee Soufer, R. Stevens, Pål Suren, James Sutcliffe, John A. Sweeney, Talkowski, Flora Tassone, Karoline Teufel, Elisabetta Trabetti, Slavica Trajkova, Trelles, Brie Wamsley, Jaqueline T. Wang, Weiss, Mullin Yu, Yuen, Jessica Zweifach.

Язык: Английский

Процитировано

1

Current landscape of fecal microbiota transplantation in treating depression DOI Creative Commons
Qi Zhang,

Yajun Bi,

Boyu Zhang

и другие.

Frontiers in Immunology, Год журнала: 2024, Номер 15

Опубликована: Июнь 25, 2024

Depression, projected to be the predominant contributor global disease burden, is a complex condition with diverse symptoms including mood disturbances and cognitive impairments. Traditional treatments such as medication psychotherapy often fall short, prompting pursuit of alternative interventions. Recent research has highlighted significant role gut microbiota in mental health, influencing emotional neural regulation. Fecal transplantation (FMT), infusion fecal matter from healthy donor into patient, emerges promising strategy ameliorate depressive by restoring microbial balance. The microbial-gut-brain (MGB) axis represents critical pathway through which potentially rectify dysbiosis modulate neuropsychiatric outcomes. Preclinical studies reveal that FMT can enhance neurochemicals reduce inflammatory markers, thereby alleviating behaviors. Moreover, shown promise clinical settings, improving gastrointestinal overall quality life patients depression. review highlights gut-brain depression need for further validate long-term safety efficacy FMT, identify specific therapeutic strains, develop targeted modulation strategies. Advancing our understanding could revolutionize treatment, shifting paradigm toward microbiome-targeting therapies.

Язык: Английский

Процитировано

5

SARSCoV‐2‐derived protein Orf9b enhances MARK2 activity via interaction with the autoinhibitory KA1 domain DOI Creative Commons

Daiki Homma,

Sophia Jobien M. Limlingan,

Taro Saito

и другие.

FEBS Letters, Год журнала: 2024, Номер unknown

Опубликована: Июль 5, 2024

Microtubule affinity‐regulating kinase 2 (MARK2) is a Ser/Thr protein that regulates cell polarity and immune responses. Here, we report Orf9b, one of the accessory proteins encoded in SARS‐CoV‐2 genome, increases MARK2 activity via interaction with autoinhibitory KAI domain. We found co‐expression Orf9b enhances HEK293 cells. does not bind to or enhance mutant form lacking KA1 lowers inhibitory phosphorylation at T595 while mutation experiments indicate this site dispensable for Orf9b‐mediated enhancement activity. Our results suggest by binding domain, which closely interacts

Язык: Английский

Процитировано

0

Innovative Drug Discovery: Targeting Cancer, Neurological Disorders, and Obesity DOI Creative Commons
Robert B. Kargbo

ACS Medicinal Chemistry Letters, Год журнала: 2024, Номер 15(9), С. 1440 - 1442

Опубликована: Авг. 21, 2024

The landscape of therapeutic innovation is rapidly evolving, with significant advances in cancer treatment, obesity management, and the modulation protein interactions neurodegenerative disorders. This Patent Highlight explores scientific breakthroughs described four recent patents covering novel compounds, advanced methods for identifying E3 ligase substrates, developing new strategies combating its related metabolic These innovations, focusing on specific molecular targets pathways, promise more effective personalized treatment options, addressing unmet needs oncology, neurology, health.

Язык: Английский

Процитировано

0