
Frontiers in Pediatrics, Год журнала: 2025, Номер 13
Опубликована: Март 18, 2025
Primary Ciliary Dyskinesia (PCD) is a rare genetic disorder affecting motile cilia, leading to impaired mucociliary clearance and increased susceptibility respiratory infections. These infections contribute long-term complications such as bronchiectasis lung function decline. This review explores both the acute impact of in children with PCD, while highlighting multiple contributors infection susceptibility. The also evaluates emerging personalized approaches gene mRNA therapy that hold promise for restoring ciliary reducing burden pediatric PCD. Acute have significant on morbidity driving progressive airway remodeling. While current treatment strategies focus managing directly, therapies targeting inflammation causes improving outcomes. Future advances medicine could further enhance therapeutic this population.
Язык: Английский