Severe toxicities in amazonian populations and the role of precision medicine in acute lymphoblastic leukemia treatment DOI Creative Commons
Luciana Pereira Colares Leitão, Natasha Monte, Juliana Carla Gomes Rodrigues

и другие.

Scientific Reports, Год журнала: 2024, Номер 14(1)

Опубликована: Ноя. 26, 2024

Abstract Corticosteroids, such as prednisone or dexamethasone, constitute integral components of antineoplastic regimens for Acute Lymphoblastic Leukemia (ALL) therapy, albeit accompanied by significant adverse effects. The multifactorial nature interindividual variability in drug response, encompassing genetic polymorphisms, underscores the complexity pharmacotherapy outcomes. However, pharmacogenetic investigations hitherto have predominantly focused on cohorts European and North American descent, thus limiting generalizability findings to populations with minimal representation. Indigenous Brazil, particularly those inhabiting Amazon region, exhibit a distinctive heritage, characterized Native ancestry. These frequently manifest suboptimal therapeutic responses elevated mortality rates following ALL treatment. Therefore, delineating molecular signatures genes implicated corticosteroid pathway within these indigenous assumes paramount importance. This study identified novel variants associated glucocorticoid Amazonian conducted comparative analyses variant frequencies across diverse global populations. underscore uniqueness groups highlight potential impact factors Precision medicine approaches tailored peculiarities emerge imperative strategies optimizing efficacy mitigating treatment-related toxicities communities.

Язык: Английский

Impact of Pharmacogenomics in Clinical Practice DOI Creative Commons
Nicola Principi,

Kyriakoula Petropulacos,

Susanna Esposito

и другие.

Pharmaceuticals, Год журнала: 2023, Номер 16(11), С. 1596 - 1596

Опубликована: Ноя. 13, 2023

Polymorphisms of genes encoding drug metabolizing enzymes and transporters can significantly modify pharmacokinetics, this be associated with significant differences in efficacy, safety, tolerability. Moreover, genetic variants some components the immune system explain clinically relevant drug-related adverse events. However, implementation dose individualization based on pharmacogenomics remains scarce. In narrative review, impact variations disposition, tolerability most commonly prescribed drugs is reported. reasons for poor everyday clinical settings are discussed. The literature analysis showed that knowledge how effectiveness, a lead to adjustment usually recommended dosages, improve reduce Despite efforts introduce practice, presently very few centers routinely use tests as guide prescription. education health care professionals seems critical keep pace rapidly evolving field pharmacogenomics. multimodal algorithms incorporate both factors prescribing could help regard. Obviously, further studies which definitively establish play role conditioning effectiveness safety needed. Many problems must solved, but advantages human fully justify all efforts.

Язык: Английский

Процитировано

10

Public preferences for pharmacogenetic testing in the NHS: Embedding a discrete choice experiment within service design to better meet user needs DOI Creative Commons
John McDermott, Videha Sharma, William G. Newman

и другие.

British Journal of Clinical Pharmacology, Год журнала: 2024, Номер 90(7), С. 1699 - 1710

Опубликована: Апрель 14, 2024

Genetic testing can be used to improve the safety and effectiveness of commonly prescribed medicines-a concept known as pharmacogenetics. This study aimed quantify members UK public's preferences for a pharmacogenetic service delivered in primary care National Health Service.

Язык: Английский

Процитировано

1

Associação da farmacogenômica com farmacogenes da superfamília citocromo P450 e os desafios de implementação na prática clínica DOI Open Access
Aline Aparecida Silva Martins, Marina Pereira Rocha

Brazilian Journal of Health Review, Год журнала: 2024, Номер 7(4), С. e71406 - e71406

Опубликована: Июль 23, 2024

A farmacogenômica representa um dos importantes pilares da medicina de precisão. Mutações em genes superfamília cytochrome P450 tem sido associadas com alteração na farmacocinética. Apesar relevância farmacogenômica, a implementação prática clínica ainda desafio. Nesse contexto, o objetivo do presente artigo foi investigar relação entre e citocromo P450. Além desafios clínica. Foi realizada uma revisão narrativa literatura partir artigos científicos disponíveis base dados pubmed publicados 2003 2023. Os família oxidase estão envolvidos metabolização 70-80% principais medicamentos utilizados. O farmacogene CYP2D6 possui grande clínica, vez que é responsável por metabolizar variedade substratos incluindo analgésicos, antidepressivos, anti-hipertensivos agentes anticancerígenos. miRNAs padrão expressão gênica membros Dados projeto Ubiquitous Pharmacogenomics demonstraram pacientes resultados quando tratados acordo as recomendações clínicas apresentaram menor porcentagem reações adversas. Contudo, apesar das evidências positivas, desafio, especialmente países desenvolvimento. inegável importância desenvolvimento científico, qual pode contribuir para futuro próximo se torne realidade dentro

Процитировано

0

Severe toxicities in amazonian populations and the role of precision medicine in acute lymphoblastic leukemia treatment DOI Creative Commons
Luciana Pereira Colares Leitão, Natasha Monte, Juliana Carla Gomes Rodrigues

и другие.

Scientific Reports, Год журнала: 2024, Номер 14(1)

Опубликована: Ноя. 26, 2024

Abstract Corticosteroids, such as prednisone or dexamethasone, constitute integral components of antineoplastic regimens for Acute Lymphoblastic Leukemia (ALL) therapy, albeit accompanied by significant adverse effects. The multifactorial nature interindividual variability in drug response, encompassing genetic polymorphisms, underscores the complexity pharmacotherapy outcomes. However, pharmacogenetic investigations hitherto have predominantly focused on cohorts European and North American descent, thus limiting generalizability findings to populations with minimal representation. Indigenous Brazil, particularly those inhabiting Amazon region, exhibit a distinctive heritage, characterized Native ancestry. These frequently manifest suboptimal therapeutic responses elevated mortality rates following ALL treatment. Therefore, delineating molecular signatures genes implicated corticosteroid pathway within these indigenous assumes paramount importance. This study identified novel variants associated glucocorticoid Amazonian conducted comparative analyses variant frequencies across diverse global populations. underscore uniqueness groups highlight potential impact factors Precision medicine approaches tailored peculiarities emerge imperative strategies optimizing efficacy mitigating treatment-related toxicities communities.

Язык: Английский

Процитировано

0