Translational Science of Rare Diseases, Journal Year: 2024, Volume and Issue: unknown

Published: Dec. 9, 2024

The 2024 International Rett Syndrome Foundation (IRSF) Scientific Meeting, held in Westminster, Colorado, gathered over 200 researchers and clinicians to discuss advancements understanding treating syndrome (RTT). Key topics included MeCP2 biology, neuronal circuitry, therapeutic development, clinical trial outcomes. meeting reinforced the importance of collaborative research unraveling RTT’s complex pathology advancing treatment approaches. With promising candidates conference underscored a growing hope for effective treatments, offering path toward improving quality life individuals with their families.

Language: Английский