Transforming Hemophilia A Care: Insights into New Therapeutic Options DOI Creative Commons
Iasmina-Maria Iurea, Emilia Severin, Alexandra Matei

et al.

Life, Journal Year: 2024, Volume and Issue: 14(12), P. 1568 - 1568

Published: Nov. 29, 2024

Hemophilia A is a hereditary bleeding disorder characterized by deficiency in clotting factor VIII, leading to significant morbidity and reduced quality of life. This review provides an updated overview the current understanding hemophilia A, highlighting its genetic underpinnings advancements treatment strategies. literature was conducted using various available databases. Relevant studies on covering genetics options, were selected summarized. Recent developments gene therapy are discussed, showcasing their potential offer long-term solutions reduce burden treatment. Additionally, addresses global disparities care policy implications, emphasizing need for comprehensive healthcare frameworks improve outcomes individuals living with worldwide. By synthesizing recent findings insights, this aims inform clinicians policymakers about evolving landscape management necessity equitable access care.

Language: Английский

Fracture Risk in People With Haemophilia A and B: A Systematic Review and Meta‐Analysis DOI Open Access
Efstathios Divaris, Ioannis Konstantinidis,

Paraskevi Karvouni

et al.

Haemophilia, Journal Year: 2025, Volume and Issue: unknown

Published: March 18, 2025

ABSTRACT Introduction Haemophilia A and B is a disease consistently associated with reduced bone mineral density, both in adults children. However, whether haemophilia also increases fracture risk has not yet been proven. Aim This systematic review meta‐analysis aimed to synthesize analyse studies evaluating the association between risk. Methods Comprehensive research was conducted three electronic databases (PubMed, CENTRAL, Scopus) up 30 June 2024. Data were expressed as relative (RR) 95% confidence intervals (CI). The I 2 index employed evaluate heterogeneity. Results Fourteen included qualitative four quantitative analysis (participants: 13,221, publication years: 2007–2022). Regarding design, five retrospective cohorts, two case‐control, seven cross‐sectional. Fracture prevalence people (PWH) 5.7%, ranging from 1.4% 27.7% (data 14 studies), compared 0.9% control group, 0% 5.1% 3 studies). In comparison healthy men, PWH demonstrated increased (RR 4.56, CI 1.28–16.25, p = 0.019, 90.74%). there insufficient data categorize fractures according their location compare incidence patients receiving prophylaxis those on‐demand treatment, well type or severity of haemophilia. Conclusion first showing more than 4‐fold general population.

Language: Английский

Citations

0

Introduction to Special Issue: Genomic Analysis of Common Disease DOI Creative Commons
Golder N. Wilson

Current Issues in Molecular Biology, Journal Year: 2025, Volume and Issue: 47(2), P. 112 - 112

Published: Feb. 10, 2025

The development of NextGen or massive parallel sequencing [...].

Language: Английский

Citations

0

Transforming Hemophilia A Care: Insights into New Therapeutic Options DOI Creative Commons
Iasmina-Maria Iurea, Emilia Severin, Alexandra Matei

et al.

Life, Journal Year: 2024, Volume and Issue: 14(12), P. 1568 - 1568

Published: Nov. 29, 2024

Hemophilia A is a hereditary bleeding disorder characterized by deficiency in clotting factor VIII, leading to significant morbidity and reduced quality of life. This review provides an updated overview the current understanding hemophilia A, highlighting its genetic underpinnings advancements treatment strategies. literature was conducted using various available databases. Relevant studies on covering genetics options, were selected summarized. Recent developments gene therapy are discussed, showcasing their potential offer long-term solutions reduce burden treatment. Additionally, addresses global disparities care policy implications, emphasizing need for comprehensive healthcare frameworks improve outcomes individuals living with worldwide. By synthesizing recent findings insights, this aims inform clinicians policymakers about evolving landscape management necessity equitable access care.

Language: Английский

Citations

0