International Journal of Molecular Sciences, Journal Year: 2025, Volume and Issue: 26(2), P. 816 - 816
Published: Jan. 19, 2025
Adeno-associated viruses (AAVs) are non-pathogenic, replication-deficient that have gained widespread attention for their application as gene therapy vectors. While these vectors offer high transduction efficiency and long-term expression, the host immune response poses a significant challenge to clinical success. This review focuses on obstacles evaluating humoral AAVs. We discuss problems with validation of in vitro tests possible approaches overcome them. Using published data neutralizing titers AAV serotypes, we built first antigenic maps AAVs order visualize relationships between varying serotypes.
Language: Английский