Quality of life considerations in myelodysplastic syndrome: not only fatigue DOI Creative Commons
Pasquale Niscola, Valentina Gianfelici, Marco Giovannini

et al.

Expert Review of Hematology, Journal Year: 2024, Volume and Issue: 17(8), P. 407 - 410

Published: July 6, 2024

KEYWORDS: myelodysplastic syndrome (MDS)quality of life (QOL)sleepphysical exerciselifestylepsychologyclinical treatment

Language: Английский

Improved survival and enhanced quality of life through anaemia correction in lower risk myelodysplastic syndromes: meaningful insights from an EUMDS Registry study DOI

Pasquale Niscola

The Lancet Haematology, Journal Year: 2025, Volume and Issue: 12(2), P. e88 - e90

Published: Feb. 1, 2025

Language: Английский

Citations

0

Research and analysis of differential gene expression in CD34 hematopoietic stem cells in myelodysplastic syndromes DOI Creative Commons
Mianzhi Wang, Chang-Sheng Liao, Xudong Wei

et al.

PLoS ONE, Journal Year: 2025, Volume and Issue: 20(3), P. e0315408 - e0315408

Published: March 12, 2025

Objective This study aims to investigate and analyze the differentially expressed genes (DEGs) in CD34 + hematopoietic stem cells (HSCs) from patients with myelodysplastic syndromes (MDS) through bioinformatics analysis, ultimate goal of uncovering potential molecular mechanisms underlying pathogenesis MDS. The findings this are expected provide novel insights into clinical treatment strategies for Methods Initially, we downloaded three datasets, GSE81173, GSE4619, GSE58831, public Gene Expression Omnibus (GEO) database as our training sets, selected GSE19429 dataset validation set. To ensure data consistency comparability, standardized sets removed batch effects using ComBat algorithm, thereby integrating them a unified gene expression dataset. Subsequently, conducted differential analysis identify significant changes levels across different disease states. In order enhance prediction accuracy, incorporated six common predictive models trained based on filtered After comprehensive evaluation, ultimately algorithms—Lasso regression, random forest, support vector machine (SVM)—as core models. more precisely pinpoint closely related characteristics, utilized aforementioned learning methods took intersection these results, yielding robust list associated features. Following this, in-depth key set validated results independently Furthermore, performed groups, co-expression enrichment delve deeper roles initiation progression. Through analyses, aim new foundations diagnosis treatment. Figure illustrates preprocessing workflow study. Results Our CD34+ revealed differences patterns compared control group (individuals without MDS). Specifically, two genes, IRF4 ELANE, were notably downregulated HSCs MDS patients, indicating their downregulatory pathological process Conclusion sheds light MDS, particular focus pivotal ELANE pathogenic genes. perspective understanding complexity exploring therapeutic strategies. They may also guide development precise effective treatments, such targeted interventions directed against

Language: Английский

Citations

0

Oral decitabine in acute myeloid leukemia: assessing efficacy, safety, and future implications for older patients DOI
Pasquale Niscola

Expert Review of Hematology, Journal Year: 2025, Volume and Issue: unknown

Published: March 31, 2025

Introduction Older patients with acute myeloid leukemia (AML) are often unsuitable for standard treatments and traditionally have a dismal prognosis. For 20 years, hypomethylating agents (HMAs), as single recently backbone venetoclax, been used in this setting. The oral combination of decitabine cedazuridine (C-DEC), which is therapeutically pharmacologically equivalent to the intravenous (IV) formulation (IV-DEC), has expanded therapeutic arsenal AML, allowing better convenience administration. This review provides an overview C-DEC, current clinical applications, ongoing studies, highlighting its potential role managing AML older patients.

Language: Английский

Citations

0

Acute Myeloid Leukemia in Older Patients: From New Biological Insights to Targeted Therapies DOI Creative Commons
Pasquale Niscola, Valentina Gianfelici, Gianfranco Catalano

et al.

Current Oncology, Journal Year: 2024, Volume and Issue: 31(11), P. 6632 - 6658

Published: Oct. 24, 2024

Acute myeloid leukemia (AML) is a heterogeneous blood-related neoplasm that predominantly afflicts older adults with poor prognosis due to their physical condition and the presence of medical accompanying comorbidities, adverse biological disease features, suitability for induction intensive chemotherapy allogenic stem cells transplantation. Recent research into molecular factors contributing development progression has led significant advancements in treatment approaches patients AML. This review article discusses latest therapeutic developments are transforming management AML adults.

Language: Английский

Citations

3

Genetic Predisposition to Myelodysplastic Syndrome: Genetic Counseling and Transplant Implications DOI
Yi Liu, Kathleen A. Calzone, Lisa J. McReynolds

et al.

Seminars in Hematology, Journal Year: 2024, Volume and Issue: unknown

Published: Sept. 1, 2024

Language: Английский

Citations

1

Latest Insights and Progress in the Clinical Management of Elderly Patients with Acute Myeloid Leukemia: From Genetic Advancements to Targeted Treatments DOI Open Access
Pasquale Niscola, Nélida I. Noguera, Valentina Gianfelici

et al.

Published: June 24, 2024

Acute myeloid leukemias (AMLs) are heterogeneous hematologic cancers that occur prevalently in older patients as the result of a complex pathobiology. The clinical outcomes with AML, often unsuitable for intensive chemotherapy and allogeneic stem cell transplantation, generally disappointing. However, recent advances understanding molecular pathogenesis other biological mechanisms recognized AML development progression have changed treatment approach, especially this particularly vulnerable category patients. Indeed, non-intensive biologically tailored approaches, such combining venetoclax hypomethylating agents, therapeutic paradigm field. Moreover, promising compounds strategies currently under advanced development. This article delves into latest management new conceptual frameworks progressively transform practice challenging setting.

Language: Английский

Citations

0

Quality of life considerations in myelodysplastic syndrome: not only fatigue DOI Creative Commons
Pasquale Niscola, Valentina Gianfelici, Marco Giovannini

et al.

Expert Review of Hematology, Journal Year: 2024, Volume and Issue: 17(8), P. 407 - 410

Published: July 6, 2024

KEYWORDS: myelodysplastic syndrome (MDS)quality of life (QOL)sleepphysical exerciselifestylepsychologyclinical treatment

Language: Английский

Citations

0